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Angelman Syndrome
Chronic Urticaria
Congenital Rubella Syndrome
Epidermolysis Bullosa
Friedreich’s Ataxia
GM2 (Tay-Sachs and Sandhoff), GM1, Canavan
Hypoxic Ischemic Encephalopathy
Limb-Girdle Muscular Dystrophy
Narcolepsy
Pitt Hopkins Syndrome
Pituitary Tumor Survivors
Prader-Willi Syndrome
Recurrent Pericarditis
Wolf Hirschhorn Syndrome
Chromosome 8P Disorders
PANS, PANDAS, AE
Barth Syndrome
CMTC and Vascular Malformations
TREND Partners
The Chion Foundation
Cure Tay-Sachs Foundation
Friedrich's Ataxia Research Alliance
Liv 4 the Cure
Team Hopefull
Joy
National Tay-Sachs & Allied Diseases Association
The Mac Pact
Pitt Hopkins Research Foundation
COMBINEDBrain
TREND Clients
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Rhythm
Harmony Biosciences